Submitted by 29PiecesOfSilver t3_yqxoei in science
bigglyboblee t1_ivv2xio wrote
Reply to comment by [deleted] in In a first, doctors treat fatal genetic disease before birth by 29PiecesOfSilver
You can read the paper if you’re interested, from my skim she has to receive injections every couple weeks for the rest of her life.
I don’t see how a single dose would work for enzyme replacement therapy, but I am not an expert in this topic.
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